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6 Hits
Search Condition : Filter (MeSH = Genetic Therapy* / methods)
Species
Resource
RRC ID
Title
Journal
Published
Link
Altmetric score
Mice
RBRC00532
87468
Targeted editing of the 21-hydroxylase locus confers durable therapeutic effect in a murine model of congenital adrenal hyperplasia.
Mol Ther
2026-2-4
Pubmed
Full text
Human and Animal Cells
293T(RCB2202)
82184
Optimization of HITI-Mediated Gene Insertion for Rhodopsin and Peripherin-2 in Mouse Rod Photoreceptors: Targeting Dominant Retinitis Pigmentosa.
Invest Ophthalmol Vis Sci
2024-11-4
Pubmed
Full text
Human and Animal Cells
HUDEP-2(RCB4557)
77307
In Vivo HSC Gene Therapy Using a Bi-modular HDAd5/35++ Vector Cures Sickle Cell Disease in a Mouse Model.
Mol Ther
2021-2-3
Pubmed
Full text
Human and Animal Cells
BHK-21
64685
Utilization of a novel Sendai virus vector in ex vivo gene therapy for hemophilia A.
Int J Hematol
2021-4-1
Pubmed
Full text
Human and Animal Cells
MDA-MB-453(RCB1192)
,
MCF7(RCB1904)
63256
Development of New Oncolytic Virotherapy Targeting Breast Cancer Using Coxsackievirus B3.
Anticancer Res
2021-1-1
Pubmed
Full text
DNA material
pCALwL (RDB1679)
12036
Targeted gene therapy toward astrocytoma using a Cre/loxP-based adenovirus system.
Brain Res
2006-4-7
Pubmed
Full text