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論文 - 一覧

  • 7 Hits
  • 検索条件 : 絞込み (MeSH = gamma-Globins / genetics)
生物種 リソース名 タイトル
ヒト・動物細胞 HUDEP-2(RCB45547) Identification of small molecule agonists of fetal hemoglobin expression for the treatment of sickle cell disease.
ヒト・動物細胞 HUDEP-2(RCB4557) Editing a γ-globin repressor binding site restores fetal hemoglobin synthesis and corrects the sickle cell disease phenotype.
ヒト・動物細胞 HUDEP-2(RCB4557) Enhanced HbF reactivation by multiplex mutagenesis of thalassemic CD34+ cells in vitro and in vivo.
ヒト・動物細胞 HUDEP-1(RCB4556) , HUDEP-2(RCB4557) Pharmacologic induction of PGC-1α stimulates fetal haemoglobin gene expression.
ヒト・動物細胞 HUDEP-2(RCB4557) Base-editing-mediated dissection of a γ-globin cis-regulatory element for the therapeutic reactivation of fetal hemoglobin expression.
ヒト・動物細胞 HUDEP-1(RCB4556) , HUDEP-2(RCB4557) Transcription factor competition at the γ-globin promoters controls hemoglobin switching.
ヒト・動物細胞 HUDEP-2(RCB4557) Targeted Integration and High-Level Transgene Expression in AAVS1 Transgenic Mice after In Vivo HSC Transduction with HDAd5/35++ Vectors.