RRC ID 61903
著者 Katagami Y, Kondo T, Suga M, Yada Y, Imamura K, Shibukawa R, Sagara Y, Okanishi Y, Tsukita K, Hirayama K, Era T, Inoue H.
タイトル Generation of a human induced pluripotent stem cell line, BRCi009-A, derived from a patient with glycogen storage disease type 1a.
ジャーナル Stem Cell Res
Abstract Glycogen storage disease type 1a (GSD1a) is an autosomal recessive disorder caused by mutations of the glucose-6-phosphatase (G6PC) gene. Mutations of the G6PC gene lead to excessive accumulation of glycogen in the liver, kidney, and intestinal mucosa due to the deficiency of microsomal glucose-6-phosphatase. Human induced pluripotent stem cells (iPSCs) enable the production of patient-derived hepatocytes in culture and are therefore a promising tool for modeling GSD1a. Here, we report the establishment of human iPSCs from a GSD1a patient carrying a G6PC mutation (c.648G > T; p.Leu216 = ).
巻・号 49
ページ 102095
公開日 2020-12-1
DOI 10.1016/j.scr.2020.102095
PII S1873-5061(20)30396-2
PMID 33291009
MeSH Cell Line* Glucose-6-Phosphatase / genetics Glycogen Storage Disease Type I* / genetics Hepatocytes Humans Induced Pluripotent Stem Cells* Liver Mutation
IF 4.495
リソース情報
ヒト・動物細胞 HPS3926 Vero(RCB0001)