論文 - 詳細
RRC ID | 75949 |
---|---|
著者 | Doyle JJ, Maios C, Vrancx C, Duhaime S, Chitramuthu B, Bennett HPJ, Bateman A, Parker JA. |
タイトル | Chemical and genetic rescue of in vivo progranulin-deficient lysosomal and autophagic defects. |
ジャーナル | Proc Natl Acad Sci U S A |
巻・号 | 118(25) |
公開日 | 2021-6-22 |
DOI | 10.1073/pnas.2022115118 |
PII | 2022115118 |
PMID | 34140407 |
PMC | PMC8237633 |
MeSH | Acetophenones / pharmacology Animals Autophagy / genetics* Benzopyrans / pharmacology Biosynthetic Pathways Caenorhabditis elegans / cytology Caenorhabditis elegans / genetics* Caenorhabditis elegans Proteins / genetics Caenorhabditis elegans Proteins / metabolism* Drug Evaluation, Preclinical Frontotemporal Dementia / genetics Frontotemporal Dementia / pathology Lysosomes / genetics* Mutation / genetics Phenotype Progranulins / genetics Progranulins / metabolism* Rivastigmine / pharmacology Small Molecule Libraries / pharmacology Sphingolipids / metabolism |
リソース情報 | |
線虫 | tm985 |